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Language: en
Pages: 442
Pages: 442
Type: BOOK - Published: 2011-04-03 - Publisher: National Academies Press
Rare diseases collectively affect millions of Americans of all ages, but developing drugs and medical devices to prevent, diagnose, and treat these conditions i
Language: en
Pages: 407
Pages: 407
Type: BOOK - Published: 2014-05-26 - Publisher: Academic Press
Rare Diseases and Orphan Drugs shows that much of what we now know about common diseases has been achieved by studying rare diseases. It proposes that future ad
Language: en
Pages: 487
Pages: 487
Type: BOOK - Published: 2014-07-30 - Publisher: Royal Society of Chemistry
Orphan drugs are designated drug substances that are intended to treat rare or ‘orphan’ diseases. More than 7000 rare diseases are known that collectively a
Language: en
Pages: 418
Pages: 418
Type: BOOK - Published: 2021-11-08 - Publisher: Springer Nature
This book provides a broad overview of rare disease drug development. It offers unique insights from various perspectives, including third-party capital provide
Language: en
Pages: 286
Pages: 286
Type: BOOK - Published: 2020-11-11 - Publisher: CRC Press
In the United States, a rare disease is defined by the Orphan Drug Act as a disorder or condition that affects fewer than 200,000 persons. For the approval of "